[PDF] from upenn.eduK Ronen, O Negre, S Roth… - Molecular …, 2011 - microb230.med.upenn.edu ... Molecular Therapy 1 A lentiviral vector encoding β-globin flanked by insulator elements has been used to treat β-thalassemia (β-Thal) suc- cessfully in one human subject. ... Sites in Mice Following Therapeutic Gene Transfer to Treat β-thalassemia... Cited by 3 - Related articles - View as HTML - All 4 versions
JS Cheung, WY Au, SY Ha, D Kim… - Journal of Magnetic …, 2011 - Wiley Online Library ... Technical Note. Reduced transverse relaxation rate (RR2) for improved sensitivity in monitoring myocardial iron in thalassemia †. ... Keywords: MRI; cardiac MR; heart; RR2; thalassemia; iron overload; chelation therapy; ferritin; hemosiderin. Abstract. ... Related articles - All 2 versions
A Ruggeri, M Eapen, A Scaravadou… - Biology of Blood and …, 2011 - Elsevier ... Blood 2007;110:2749-2756. 5. Lucarelli G, Clift RA, Galimberti M, et al. Marrow transplantation for patients with thalassemia: results in class 3 patients. Blood 1996;87:2082-2088. 6. Lawson SE, Roberts IA, Amrolia P, Dokal I, Szydlo R, Darbyshire PJ. ... Cited by 2 - Related articles - All 3 versions